Good news and a novel FDA approved treatment for MPS- I Homologous stem cell therapy. Good news and a novel FDA approved treatment for MPS- I Homologous stem cell therapy. Read more: https://www.globenewswire.com/news-release/2020/07/20/2064241/0/en/Orchard-Therapeutics-Announces-Orphan-Drug-and-Rare-Pediatric-Disease-Designations-for-OTL-203-for-the-Treatment-of-MPS-I.html #RareDisease #rayofhope #OrphanDrug #FDA
