The U.S. Food and Drug Administration today announced it has awarded 18 new research grants totaling more than $19 million to boost the development of products for patients with rare...
An RNA editing technique called “exon skipping” has shown preliminary success in treating a rare and severe form of muscular dystrophy that currently has no treatment, based on a new...
British surgeons have taken a “big step forward” towards curing the most common form of blindness by developing and successfully performing a ground breaking operation. Surgeons at London’s Moorfields Eye...
Amicus Therapeutics has stepped in to snap up the late-stage rare disease biotech Scioderm, beefing up its orphan drug pipeline in exchange for $229 million in stock and cash along...
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New Delhi, 27th February, 2015: Rare Diseases Day was observed on 27th February to raise awareness about rare diseases and improve access to treatment and medical representation for individuals with...
New Delhi: The Delhi High Court Friday directed AIIMS to provide free treatment to a two-year-old boy, suffering from Gaucher’s disease, a genetic disorder. Justice Rajiv Shakdher also issued notice...
